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Our Mission
to fund research to develop a treatment—and ultimately a cure—for PURA Syndrome.
The PURA Community Gains Momentum at ASGCT 2026!
What is PURA Syndrome?
PURA syndrome is a rare genetic disorder caused by mutations
in the PURA gene
Tools for Researchers
We partner with leading institutions to provide researchers with reliable tools for studying PURA Syndrome
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Read the latest news and information about the work we do to find and fund a cure for PURA Syndrome
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